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Search Results - pamela+zeitlin
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PS-341 Rescues Cystic Fibrosis Transmembrane Regulator (CFTR) from Endoplasmic Reticulum Mediated Degradation
UNMET NEEDThere is understanding that mutations in the cystic fibrosis transmembrane regulator (CFTR) protein can lead to life-threatening illness. When functioning normally, CFTR is thought to be a necessary cAMP-activated chloride channel. In CF, this channel is thought to be misprocessed and retained in the endoplasmic reticulum of epithelial cells,...
Published: 3/13/2025
|
Inventor(s):
Neeraj Vij
,
Pamela Zeitlin
Keywords(s):
Biologics
,
Cystic Fibrosis
,
Cystic Fibrosis (CF)
,
Disease Indication
,
Genetic Disorders
,
Protein
,
Therapeutic Matter
,
Therapeutic Substance
,
Therapeutics
Category(s):
Clinical and Disease Specializations
,
Clinical and Disease Specializations > Genetic Diseases > Cystic Fibrosis
,
Clinical and Disease Specializations > Rare Diseases
,
Clinical and Disease Specializations > Respiratory Diseases
,
Technology Classifications > Therapeutic Modalities > Proteins
,
Technology Classifications > Therapeutic Modalities > Small Molecules
,
Clinical and Disease Specializations > Genetic Diseases
,
Technology Classifications > Therapeutic Modalities
S9
C04772: S9, A Cystic Fibrosis bronchial epithelial cell line Technical Details: Cystic Fibrosis bronchial epithelial cell line isolated from a patient with genotype ?508 /W1282X. IB3-1 Cells were immortalized with adeno12SV0 and later infected with a viral vector AAV carrying CFTR full length.Looking for Partners: This cell line may be useful in...
Published: 3/13/2025
|
Inventor(s):
William Guggino
,
Terence Flotte
,
Pamela Zeitlin
Keywords(s):
Basic Research Biomarker
,
Cell Model
,
Cystic Fibrosis
,
Cystic Fibrosis (CF)
,
Discovery/Research Tools
,
Disease Indication
,
Epithelial Cells
,
Genetic Disorders
,
In Vitro Research Tool
Category(s):
Clinical and Disease Specializations
,
Clinical and Disease Specializations > Genetic Diseases > Cystic Fibrosis
,
Clinical and Disease Specializations > Rare Diseases
,
Clinical and Disease Specializations > Respiratory Diseases
,
Technology Classifications > Research Tools > Cell Lines
,
Clinical and Disease Specializations > Genetic Diseases
,
Technology Classifications > Research Tools
C38
C04744: C38 Technical Details: JHU scientists have created a Cystic Fibrosis bronchial epithelial cell line that was isolated from a patient with genotype ?508/W1282X. Cells were immortalized with adeno12SV0 and later transfected with a cDNA from AAV carrying CFTR truncated for the first 119 amino acids.Looking for Partners: This cell line may be...
Published: 3/13/2025
|
Inventor(s):
Pamela Zeitlin
,
William Guggino
,
Terence Flotte
Keywords(s):
Adeno-Associated Virus
,
Basic Research Biomarker
,
Cell Model
,
Cystic Fibrosis
,
Cystic Fibrosis (CF)
,
Discovery/Research Tools
,
Disease Indication
,
Epithelial Cells
,
Genetic Disorders
,
In Vitro Research Tool
,
Research Reagent
,
Translational Research Biomarker
,
Viruses
Category(s):
Clinical and Disease Specializations
,
Clinical and Disease Specializations > Genetic Diseases > Cystic Fibrosis
,
Clinical and Disease Specializations > Rare Diseases
,
Clinical and Disease Specializations > Respiratory Diseases
,
Technology Classifications > Research Tools > Cell Lines
,
Technology Classifications > Research Tools > Viruses
,
Clinical and Disease Specializations > Genetic Diseases
,
Technology Classifications > Research Tools
IB3-1
C04681: IB3-1 Technical Details: Cystic Fibrosis bronchial epithelial cell line isolated from a patient with genotype ?F508 /W1282X. Cells were immortalized with adeno12SV0.Looking for Partners: This cell line will be useful for the identification of drugs that treat cystic fibrosis.Publications Am J Physiol Cell Physiol. 2000 Feb;278(2):C259-67Sin...
Published: 3/13/2025
|
Inventor(s):
William Guggino
,
Pamela Zeitlin
Keywords(s):
Adeno Virus
,
Basic Research Biomarker
,
Cell Model
,
Cystic Fibrosis
,
Cystic Fibrosis (CF)
,
Discovery/Research Tools
,
Disease Indication
,
Epithelial Cells
,
Genetic Disorders
,
In Vitro Research Tool
,
Research Reagent
,
Viruses
Category(s):
Clinical and Disease Specializations
,
Clinical and Disease Specializations > Genetic Diseases > Cystic Fibrosis
,
Clinical and Disease Specializations > Rare Diseases
,
Clinical and Disease Specializations > Respiratory Diseases
,
Technology Classifications > Research Tools > Cell Lines
,
Technology Classifications > Research Tools > Viruses
,
Clinical and Disease Specializations > Genetic Diseases
,
Technology Classifications > Research Tools
A p105-based NF-(kappa) B Super repressor
C04290: A p105-based NF-(kappa) B Super repressor Technical Details: Nuclear factor (NF)-kB is a family of transcription factors that regulate immune and inflammatory responses, programmed cell death (apoptosis), and developmental processes. In normal cells, NF-kB is latent, and is activated transiently by stimuli and stresses. However, under pathological...
Published: 3/13/2025
|
Inventor(s):
Li Lin
Keywords(s):
Biologics
,
Cancers
,
Chemotherapy
,
Disease Indication
,
Nucleic Acid
,
Single
,
Skin Cancer
,
Therapeutic Matter
,
Therapeutic Substance
,
Therapeutics
,
Therapy Type
Category(s):
Clinical and Disease Specializations
,
Clinical and Disease Specializations > Dermatology
,
Clinical and Disease Specializations > Oncology > Skin Cancer
,
Technology Classifications > Therapeutic Modalities > Gene Therapies
,
Technology Classifications > Therapeutic Modalities > Proteins
,
Technology Classifications > Therapeutic Modalities > Targets
,
Clinical and Disease Specializations > Oncology
,
Technology Classifications > Therapeutic Modalities
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